STAT+: Pharmalittle: در حال خواندن یک داروی بیماری نادر Regeneron، یک ژن درمانی Ultragenyx و موارد دیگر هستیم.

STAT+: Pharmalittle: We’re reading about a Regeneron rare disease drug, an Ultragenyx gene therapy, and more

A Regeneron drug for an ultra-rare disease that causes bone to grow where it shouldn't won U.S. regulatory approval, capping a three-decade effort